Cajal Therapeutics is developing novel medicines for serious diseases, including anemias of inflammation, neurodegenerative diseases, and other iron-related disorders.



Iron homeostasis is vital for cellular and systemic energy, oxygen transport, and brain function. Loss of iron homeostasis, whether deficiency or overload, can drive dysfunction across organs and systems. Cajal is developing novel therapies to restore iron balance and open new paths to treat disease.

We are developing small molecule and RNA medicines that restore iron homeostasis across systemic and neurologic diseases. Our lead program, CTX001, is a first-in-class iron mobilizer designed to restore iron transport and make iron available again to key metabolic and cellular processes.
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