Advancing medicines to restore homeostasis

Cajal Therapeutics is developing novel medicines for serious diseases, including anemias of inflammation, neurodegenerative diseases, and other iron-related disorders.

Iron at the core of health and disease

Iron homeostasis is vital for cellular and systemic energy, oxygen transport, and brain function. Loss of iron homeostasis, whether deficiency or overload, can drive dysfunction across organs and systems. Cajal is developing novel therapies to restore iron balance and open new paths to treat disease.

Advancing novel medicines to restore homeostasis

We are developing small molecule and RNA medicines that restore iron homeostasis across systemic and neurologic diseases. Our lead program, CTX001, is a first-in-class iron mobilizer designed to restore iron transport and make iron available again to key metabolic and cellular processes.

Our pipeline

Transform the future with us

“All outstanding work, in art as well as in science, results from immense zeal applied to a great idea.”